Proturon schreef op 17 augustus 2021 13:11:
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En waarom zou deze rhGAA ook niet uit de koeien gehaald kunnen worden ?
Is dat alleen maar de konijnen voorbehouden.....
Ter verduidelijking, rhGAA kwam (komt ) al uit konijnen
Pompe's disease is a fatal muscular disorder caused by lysosomal alpha-glucosidase deficiency. In an open-label study, four babies with characteristic cardiomyopathy were treated with recombinant human
alpha-glucosidase (rhGAA) from rabbit milk at starting doses of 15 mg/kg or 20 mg/kg, and later 40 mg/kg. The enzyme was generally well tolerated. Activity of alpha-glucosidase normalised in muscle. Tissue morphology and motor and cardiac function improved. The left-ventricular-mass index decreased significantly. We recommend early treatment. Long-term effects are being studied.